Breakthrough Gene Therapy to Cure Hemophilia A: A New Era of Treatment
Hemophilia A, a hereditary bleeding disorder caused by the deficiency of clotting Factor VIII, has long been a challenge for the medical community. With patients often requiring lifelong injections of clotting factors, treatment remains both costly and inconvenient. However, Indian scientists have recently achieved a groundbreaking milestone by successfully testing a gene therapy technique aimed at curing severe Hemophilia A. This innovative approach promises a one-time treatment that could revolutionize the lives of thousands of patients worldwide. Understanding Hemophilia A Hemophilia A is a genetic disorder characterized by the deficiency or malfunction of Factor VIII, an essential protein involved in blood clotting. Patients with severe hemophilia have less than 1% of the normal clotting factor levels, making them prone to spontaneous and potentially life-threatening bleeding episodes. Global and National Impact India has the second-largest hemophilia patient pool globally, with e...